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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
DHPR α1S
Energy Metabolism/drug effects
Gene Expression Regulation/drug effects
Base Sequence
Muscular Dystrophy
Mice
Dynamin 2
Mitochondrial fission
Diseases
Inhibitors
Multi exon skipping
Génomique
Myogenesis
Dystrophin-EGFP
Calcium
Homeostasis
Activin Receptors
Immunoglobulin Fc Fragments/pharmacology
Ex-vivo
Dystrophine
Calcium Channels
Liver
Mdx mouse
Cachexia
Dystrophin central domain
Morphogenesis
NNOS
Hepatocellular carcinoma
CD38
Muscle Strength
Animal/physiopathology
CaVβs
Molecular docking
Long noncoding RNA
Invivo
CaV subunits
Duchenne muscular dystrophy DMD
Dystrophin
Cardiomyopathie
Animals
Exon skipping
Becker muscular dystrophy BMD
Muscular Atrophy
Metabolism
Clinical trials
Delivery
CTNNB1
Inbred C57BL
BMD
Duchenne muscular dystrophy
Becker muscular dystrophy
Dystrophie Musculaire de Duchenne DMD
Cardiomyopathy
Muscle development
Drp1
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
LKB1
LncARN
Antisense oligonucleotides
Molecular Sequence Data
Skeletal muscle
Multi resolution modeling
Muscles/physiopathology
Genomic
Inbred mdx
Dystrophy
Duchenne DMD dystrophy
Cultured
Human Umbilical Vein Endothelial Cells
Hear
Epigenetics
Cells
MES
MiARN
Humans
Allele‐specific silencing therapy
Becker BMD muscular dystrophy
Cell homeostasis
Knockout
Long QT
Autophagy
Dystrophie Musculaire de Becker BMD
DMD
Muscular dystrophy
Cell Biology
Male
Gene expression
LncRNA
Centronuclear myopathy
Myotendinous junction
Modificateurs de gènes
Cell Line
Muscle
Muscle Biology
DMO
Dystrophie musculaire de Becker
NAD+
L-Type
Multiresolution modeling
Gene modifiers