PPMO pre-treatment is beneficial for AAV-based gene therapy in Duchenne Muscular Dystrophy

Anne Forand (1, 2) , Antoine Muchir (1) , Nathalie Mougenot (3) , Caroline Sevoz-Couche (4) , Cécile Peccate (1) , Mégane Lemaitre (3) , Mathew Wood , Stéphanie Lorain (1) , France Pietri-Rouxel (1)

1 Centre de recherche en Myologie – U974 SU-INSERM
2 Inovarion
3 UMS28 - Phénotypage du petit animal
4 UMRS 1158 - Neurophysiologie Respiratoire Expérimentale et Clinique

Domaines: Sciences du Vivant [q-bio]

Anne Forand, Antoine Muchir, Nathalie Mougenot, Caroline Sevoz-Couche, Cécile Peccate, et al.. PPMO pre-treatment is beneficial for AAV-based gene therapy in Duchenne Muscular Dystrophy. Myologie 2019, Mar 2019, Bordeaux, France. ⟨hal-03996969⟩